Browsing by Subject "Enzyme replacement therapy"
Now showing items 1-6 of 6
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Alternative laronidase dose regimen for patients with mucopolysaccharidosis I: a multinational, retrospective, chart review case series
| Date Issued: 2016A terapia de reposição enzimática (TRE) com laronidase (α-L-iduronidase humana recombinante, Aldurazyme®) é indicada para sinais e sintomas não neurológicos da mucopolissacaridose tipo I (MPS I). O regime de dose de ... -
Respiratory function during enzyme replacement therapy in late-onset Pompe disease: longitudinal course, prognostic factors, and the impact of time from diagnosis to treatment start
| Date Issued: 2020OBJETIVO: Examinar a função muscular respiratória entre pacientes com doença de Pompe de início tardio (LOPD) no Registro de Pompe (NCT00231400 / Sanofi Genzyme) durante terapia de reposição enzimática (TRE) com alglucosidase ... -
Taliglucerase alfa in Gaucher disease: Description of a Brazilian experience
| Date Issued: 2018