Browsing by Subject "Late-onset Pompe disease"

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Respiratory function during enzyme replacement therapy in late-onset Pompe disease: longitudinal course, prognostic factors, and the impact of time from diagnosis to treatment start

Stockton, David W. et al. | Date Issued: 2020

OBJETIVO: Examinar a função muscular respiratória entre pacientes com doença de Pompe de início tardio (LOPD) no Registro de Pompe (NCT00231400 / Sanofi Genzyme) durante terapia de reposição enzimática (TRE) com alglucosidase ...